Pharmacokinetic and Early Efficacy of OPT101 in Patients With Type 1 Diabetes Mellitus
A 48-week Phase 2 Multicenter Controlled Pharmacokinetic and Pilot Efficacy Trial of Subcutaneous OPT101 in Patients With Recent Onset Type 1 Diabetes Mellitus
Who can join
As published by the study on ClinicalTrials.gov. "Not stated" means the study hasn't said — ask the study team.
- Age
- 18 Years to 50 Years
- Sex
- All sexes
- Healthy volunteers
- Not accepted
- Compensation
- Not stated
Other requirements are listed under Eligibility below. Only the study team can confirm whether you can join.
What to expect
No one can promise a trial will help you personally — that is what the research is trying to find out.
What participation involves
- Time periods mentioned: 2 weeks, 1 year
- Procedures mentioned: Injections
Only what the study's summary and detailed description on ClinicalTrials.gov say. Time periods may describe the whole study or a part of it — ask the study team what applies to you.
Show the study's own words
- "This study will examine the safety of three times weekly SC injections of OPT101 at each of three dose levels over two weeks as well as one year of treatment with SC OPT101 or placebo to match at a single dose level."
- "This multipart study begins with an open label exploration of tolerance and pharmacokinetics of subcutaneously (SC) administered OPT101, given at increasing doses of 1.0, 1.5, or 2.0 mg/kg three times per week for two weeks to separate sequential cohorts of six adult patients (n=18 total) diagnosed with type 1 diabetes mellitus within 20 years of screening."
- "In Part B, the highest tolerated dose will then be tested over one year in a total of n=27 subjects having C-peptide 0.2 ng/ml, with 12 diagnosed within 1 to 5 years of screening, and 15 diagnosed within \>5 to 10 years."
- "Subjects will be randomized to treatment or control in a 2:1 ratio and will be treated for one year."
- Compensation
- Not stated
- Study-related exams and procedures are typically provided at no cost. This is how many trials work in general — confirm the details for this study with the study team.
- Participants are monitored closely by the research team throughout the study.
- Some participants may receive access to an investigational treatment, which is still being studied.
- Your participation helps researchers learn whether this approach could help future patients.
About this study
In plain language
This study tests the safety of OPT101 in adults ages 18 to 50 with type 1 diabetes. It tests shots under the skin three times a week at three dose levels over two weeks. It also tests one year of OPT101 or placebo, a shot with no study drug, at one dose level.
This study will examine the safety of three times weekly SC injections of OPT101 at each of three dose levels over two weeks as well as one year of treatment with SC OPT101 or placebo to match at a single dose level.
Compensation is read from the study's own description and may be missing — always confirm with the study team.
Eligibility
Who can join
- Be 18 to 50 years old and able and willing to give informed consent. Parts B and C need separate consent.
- Agree to wear a continuous glucose monitor, a device that tracks blood sugar, throughout the study.
- Have type 1 diabetes diagnosed within 20 years for Part A, 1 to 10 years for Part B, or within 1 year for Part C.
- For Parts B and C, have a lab test showing Th40 cells make up at least 35% of certain immune cells.
- Have stable health based on an exam, health history, blood tests, and vital signs.
- If you can become pregnant, have negative blood and urine pregnancy tests before treatment.
- If you can become pregnant, use hormonal birth control, an IUD, or two barrier methods during the study.
- Men with female partners must use two barrier birth control methods unless their partner uses hormonal birth control or an IUD.
Who can't join
- Have cancer or a history of cancer, except basal cell skin cancer or squamous cell skin cancer that has not spread beyond its starting layer.
- Have a weak immune system, a disease causing low immune cell counts, a bone marrow or organ transplant, or current treatment that changes how the immune system works.
- Have stage 2 or worse kidney disease, certain abnormal kidney, liver, blood cell, or blood-clotting tests, or a body mass index (BMI) below 20 or above 35.
- Have a history of blood clots, heart attack, stroke, mini-stroke, or clotting disorders; recent surgery or lack of movement; recent bleeding or a bleeding disorder; or cannot safely receive blood thinners. Planned non-urgent procedures or surgery through follow-up also rule you out.
- Have an active, long-term, or repeated infection, be prone to infections, or have an open, draining, or infected wound that will not heal. Recent or active hepatitis A, current or long-term hepatitis B or C, HIV, or any history of tuberculosis also rule you out. Immunity to hepatitis B from a past infection or vaccine is allowed.
- Received a live, weakened vaccine in the past 60 days, or plan to receive one during the study or within 60 days after the last dose. A history of allergy to antihistamines also rules you out.
- Be pregnant or breastfeeding, or plan to become pregnant or father a child during the study or within 120 days after the last dose.
- Have active drug or alcohol abuse in the past year or a positive required drug test; be in another study of an experimental drug or device or have joined one too recently; be a prisoner; or have another health condition the study doctor thinks could make participation unsafe or difficult.
Simplified for readability. The official criteria below are what the study team uses.
Official eligibility criteria
Inclusion Criteria: * 1\. Able and willing and able to give informed consent for the trial (separate consent must be obtained for Parts B or C). 2\. Willing to wear a continuous glucose monitor for the duration of the trial (e.g., Freestyle Libre 3). 3\. Male or female aged ≥18 to 50 years on the day of signing informed consent. 4. Diagnosis of T1DM within the last 20 years for Part A, within 1 to 10 years \[N=15 at \>5 to 10, N=12 at 1 to 5 yrs\] for Part B, within less than or equal to 1 year for Part C. 5\. For Parts B and C only, T-cell phenotype Th40 level greater than or equal to 35% of CD3+ leukocytes (performed at the OPT lab). 6\. Is medically stable based on physical examination, medical history, laboratory results, and vital signs performed at screening. 7\. Women of childbearing potential (WOCBP) must have a negative highly sensitive serum test (beta- human chorionic gonadotropin) at screening and a negative urine pregnancy test at the Visit 1 Day 1 prior to receiving the investigational product. 8\. WOCBP must agree to use one of the following methods of birth control for the duration of the clinical trial: Systemic hormonal contraceptive (oral, injected, transdermal), intrauterine device, double barrier (e.g., cervical cap or diaphragm with condom or spermicide). Men with female partners must agree to use double barrier contraception, unless their partner is using systemic hormonal contraceptives or has an intrauterine device. Exclusion Criteria: * 1\. Current malignancy or history of malignancy other than basal cell carcinoma or squamous cell carcinoma in situ. 2\. Has an immune deficiency syndrome (for example, severe combined immunodeficiency syndrome, T-cell deficiency syndromes, B-cell deficiency syndromes, or chronic granulomatous disease), or bone marrow or organ transplantation, or a disease associated with lymphopenia. 3\. Has chronic kidney disease of Stage 2 or higher with eGFR of \<90 mL/min/1.73m2. 4\. Is currently receiving an immuno-modulatory treatment. 5. Patients with a history of venous and arterial thromboembolic events including, but not limited to, the following: 1. Deep venous thrombosis, pulmonary embolism, myocardial infarction, stroke, transient ischemic attack, or arterial insufficiency causing digital gangrene. 2. Patients with recent immobilization or recent surgery. 3. Patients with a history of abnormal prothrombotic laboratories such as congenital or inherited deficiency of antithrombin III, protein C, protein S, or confirmed diagnosis of antiphospholipid syndrome. 6\. Has an active infections, is prone to infections or has chronic, recurrent or opportunistic infectious disease, including but not limited to, Epstein-Barr virus, cytomegalovirus, chronic renal infection, chronic chest infection, sinusitis, recurrent urinary tract infection, Pneumocystis carinii pneumonia, aspergillosis, latent or active granulomatous infection, histoplasmosis, or coccidioidomycosis or an open, draining, or infected non-healing skin wound or ulcer. 7\. Has recent or active hepatitis A infection, current/chronic hepatitis B and hepatitis C infection, or HIV infection. Participants with immunity to hepatitis B from previous infection, defined as negative HBsAg, positive anti-HBc, and positive hepatitis B surface antibody \[anti-HBs\] or vaccination \[defined as negative HBsAg, negative anti-HBc, and positive anti-HBs\] are eligible to participate. 8\. Has a history of latent or active tuberculosis. 9. Has received a live attenuated vaccine within the last 60 days including patients who plan to receive live attenuated vaccines during the study or within 60 days after the final dose of study treatment. 10\. Patients with the following should be excluded: <!-- --> 1. Abnormal coagulation test at screening: prothrombin time (PT; \>14 sec), activated partial thromboplastin time (aPTT; \>32 sec) or fibrinogen level (\<190 or \>450 mg/dL). 2. Abnormal liver function tests (except in the case of known Gilbert's syndrome): i. AST or ALT ≥3x ULN and total bilirubin ≥2x ULN ii. AST or ALT ≥5x ULN iii. Abnormal platelet counts (\<150 or \> 450 x10 to the third/uL) iv. Abnormal white blood cell counts (\< 3.0 or \>11.0 x10 to the third/uL ) v. Abnormal eGFR (\< 90 mL/min) vi. Abnormal Factor VIII (\<50% or \>150% of normal) vii. Abnormal D-Dimer (\> 500 ng/mL of fibrinogen equivalent units (FEU)) 11. Patients planning to undergo elective procedures or surgeries at any time after signing the ICF through the follow-up visit. 12\. Is pregnant or breastfeeding or expecting to conceive or father children within the projected duration of the trial, starting with the screening visit through 120 days after the last dose of trial treatment. 13\. Recent history of bleeding or bleeding disorders or any condition whereby in the opinion of the treating investigator giving anti-coagulation during treatment would be contraindicated. 14\. History of hypersensitivity to antihistamines. 15. Body mass index \<20 or \>35 kg/M2 16. Patients with active drug or alcohol abuse within one year prior to screening or patients who test positive for required drug testing during screening (refer to §8.4). 17\. Patient is participating in a clinical trial of another investigational drug or device, including patients who have participated in another study for duration of 5 half-lives of the investigational agent. 18\. Patient is a prisoner. 19. Patients with any medical condition, including, but not limited to, cardiac, endocrinologic, hematologic, hepatic, immunologic, metabolic, urologic, pulmonary, neurologic, dermatologic, renal, or a psychiatric condition that, in the opinion of the Investigator, could compromise their ability to participate in this study.
Study sites (5)
AL
- University of Alabama at Birmingham - Department of Medicina · Birmingham, AL 35294Lisa Boswell · Study contact · (303) 503-9954 · lb@op-t.comMore trials in Birmingham
CA
- Diablo Clinical Research Center · Walnut Creek, CA 94598Lisa Boswell · Study contact · (303) 503-9954 · lb@op-t.comMore trials in Walnut Creek
CO
- Barbara Davis Center - University of Colorado Anschuttz Medical Campus · Aurora, CO 80045Lisa Boswell · Study contact · (303) 503-9954 · lb@op-t.comMore trials in Aurora
IL
- University of Chicago Medical Center · Chicago, IL 60637Lisa Boswell · Study contact · (303) 503-9954 · lb@op-t.comMore trials in Chicago
WA
- Rainier Clinical Research Center · Renton, WA 98057Lisa Boswell · Study contact · (303) 503-9954 · lb@op-t.comMore trials in Renton